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Oral Drug for Thalassemia Anaemia
January 6 , 2026
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- The US Food and Drug Administration (FDA) approved the first oral pill for treating anaemia in adult thalassemia patients.
- The approved drug is Mitapivat.
- It is approved for both transfusion-dependent and non-transfusion-dependent alpha- and beta-thalassemia.
- Mitapivat works as a pyruvate kinase activator, improving red blood cell survival and increasing haemoglobin levels.
- The drug reduces dependence on regular blood transfusions.
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